Thalassemia and Sickle Cell Anaemia are common genetic disorders, with options for treatment and prevention available.

Insertion One or more extra nucleotides are inserted into replicating DNA, often resulting in a frameshift One form of beta-thalassemia ... fibrosis Chromosomal mutation Inversion One region ...

and transfusion dependent beta-thalassemia (TDT), positioning Abu Dhabi as a leading destination for life sciences and is a significant achievement in the field of innovation and gene therapies.

This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD) and transfusion dependent beta-thalassemia (TDT), positioning Abu Dhabi as a ...