Citrullination, a transformative protein post-translational modification, is gaining recognition for its wide-ranging impact ...

Many diseases are caused by dysfunctional gene expression that leads to too much or too little of a given protein. Efforts to ...

Gene syntax also affects the behavior of genetic circuits, and contributes to unpredictable outcomes in genetic networks.

Researchers at Tokyo University of Science have developed Chol-HDOs, which efficiently penetrate the brain, overcoming ...

A major new initiative was launched on Tuesday (15 April) by the Wellcome Sanger Institute in collaboration with Pacific ...

Getting therapeutic drugs past the blood-brain barrier has long been a major challenge in treating brain diseases. Now, researchers have explored how cholesterol-modified heteroduplex oligonucleotides ...

ATSN-201 was given regenerative medicine advanced therapy designation to treat X-linked retinoschisis, for which there ...

The DecisionDx-Melanoma test accurately identifies low sentinel lymph node risk in melanoma, according to the DECIDE study.

Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...

In the first comprehensive, cell-by-cell analysis of brain tissue from individuals with Tourette syndrome, researchers have ...

Aug. 7, 2024 — Bioengineers have developed a noninvasive tool to measure gene expression and gene therapy delivery in specific brain regions using ... New Gene Therapy Approach Shows Promise for ...

A study published in the American Journal of Human Genetics by researchers at Baylor College of Medicine and the Jan and Dan Duncan Neurological Research Institute (Duncan NRI) at Texas Children's ...