Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...

Cancer Gene Therapy is the essential gene and cellular therapy resource for cancer researchers and clinicians, keeping readers up to date with the latest developments in gene and cellular ...

Medics in the UK have become the first in the world to successfully administer a pioneering gene therapy that preserves sight ...

This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first ...

Factor VIII gene was introduced into hematopoietic stem cells in men with hemophilia. The annualized bleeding rate went from 10 to 0. No worrisome gene integrations were seen. The content of this ...

Christmas has come a few days early for Spark Therapeutics after the FDA approved its ground-breaking gene therapy for a rare eye disease. It looked likely that the FDA would approve the US ...

Understand the critical steps involved in translating laboratory research into clinical-grade cell and gene therapies. Explore how innovations in cell and gene therapy are paving the way for more ...

CSL Behring has shared positive four-year results from a late-stage study of its haemophilia B gene therapy Hemgenix ...

A second gene therapy candidate that spurs antigen-specific ... following myocardial infarction was deemed due to a previous history of coronary artery disease and severe aortic stenosis rather ...