Hunter syndrome is an exceedingly rare genetic disorder caused by a malfunctioning or missing enzyme. Patients with Hunter ...

Betsy Arakawa — the classical pianist married to Gene Hackman — died last month of hantavirus pulmonary syndrome, a rare ...

The UK regulatory authorities have approved the first ever trial of a revolutionary gene therapy for young children diagnosed with Hunter syndrome, a devastating rare lysosomal storage disorder. Five ...

The Hunter syndrome program was developed by Brian Bigger, a professor of cell and gene therapy at The University of Manchester. Professor Bigger has published preclinical data demonstrating that the ...

The cause of death for Betsy Arakawa, actor Gene Hackman's wife, was revealed to be hantavirus pulmonary syndrome, a rare ...

Officials said Friday that Betsy Arakawa, the wife of Academy Award-winning actor Gene Hackman, died of hantavirus pulmonary ...

Shire’s attempts to develop a drug for cognitive impairment from the rare inherited disease Hunter Syndrome has failed to produce results. The company’s Elaprase (idursulfase) is already ...

Worries about hantavirus are spreading online after news broke that the late Gene Hackman's wife, Betsy Arakawa, had passed ...

GC Biopharma announced on the 5th that the Ministry of Food and Drug Safety has designated the treatment for severe Hunter syndrome, 'Hunterase ICV (intracerebroventricular),' as an orphan drug.

Denali remains on track to submit a BLA for tividenofusp alfa or DNL310 for the treatment of MPS II (Hunter syndrome), under the accelerated approval pathway in early 2025, and is preparing for a ...

Hunter was born with Childhood onset Heart Disease (CoHD), with two holes in the chambers of her tiny heart. The congenital ...