President Trump yesterday announced a baseline tariff of 10% on all imported products and higher rates on certain countries ...

One of the demands raised during the protests was access to 'Elevidys', a one-time gene therapy treatment that has the ...

The European Medicines Agency asked for three clinical trials to be placed on hold until the exact cause of death of a US ...

Sarepta stock tumbled Thursday after European officials put all studies of the company's gene therapy, Elevidys, on hold.

Since he was a young child, Aaron Kondo has lived with muscular dystrophy. A popular history teacher at Maui High School for ...

Muscular Dystrophy Association (MDA) has teamed up with Burn Boot Camp, a leading boutique fitness franchise, for the 9th annual national 'Be Their Muscle' philanthropic event. Throughout April, over ...

Charley Seckler has found "humor in the madness" of rolling through life with a rare disease. He drops a blog post weekly, ...

An 8-year-old northern Minnesota boy is one of the first in the country to receive a specific type of gene therapy treatment.

The Cambridge-based biotech's experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, ...

Muscular Dystrophy Association family members and Burn Boot Camp leadership are making a difference kicking off the 9th annual ‘Be Their Muscle’ campaign. CHARLOTTE, N.C., March 31, 2025 ...

Epicrispr has raised $68m in the initial close of its Series B financing round to commence the clinical trial of EPI-321 for ...