Mum's fear for son with rare and unpredictable condition
had never heard of Neurofibromatosis type 1 (NF1) until her son Tom was diagnosed just before his second birthday. The now-10 ...
Kaleido Scope5 年
NF108: Binimetinib Study
This is a phase II open label study that will evaluate children ≥ 1 year of age and adults with neurofibromatosis type 1 (NF1) and plexiform neurofibromas treated with the MEK inhibitor, binimetinib.
Cuba Headlines15 天
U.S. Denies Humanitarian Visa to Cuban Child Damir Due to MINSAP Bureaucracy
The U.S. Embassy in Havana has refused a humanitarian visa for Damir Ortiz Ramírez, a 10-year-old Cuban boy suffering from neurofibromatosis type 1 ...
Cuba Headlines10 天
Cuban Woman Holds Solo Protest Outside Havana Hospital for Damir's Health: "This Is Why We ...
A Cuban woman staged a solitary protest outside the "Juan Manuel Márquez" Pediatric Hospital in Havana, demanding medical care for 10-year-old Damir ...
MedPage Today11 天
FDA OKs Mirdametinib for Neurofibromatosis Type 1
Opens in a new tab or window The FDA on Tuesday approved mirdametinib (Gomekli) for adults and kids ages 2 and up with neurofibromatosis type 1 (NF1). Approval of the MEK inhibitor is specifically ...
The American Journal of Managed Care10 天
FDA Approves Mirdametinib for Neurofibromatosis Type 1 With Plexiform Neurofibromas
Moertel CL, Hirbe AC, Shuhaiber HH, et al. ReNeu: A pivotal phase 2b trial of mirdametinib in children and adults with neurofibromatosis type 1 (NF1)-associated symptomatic inoperable plexiform ...
MedCity News10 天
FDA Approval of Drug for Rare Tumors Enables SpringWorks to Challenge AstraZeneca
The disease, neurofibromatosis type 1 (NF1), is technically not cancer as the tumors that form are benign. But NF1 can lead to cancers. Even if a patient’s tumors aren’t cancerous, they are ...