There are approximately 7,000 different types of rare disease and researchers estimate that there are more than 300 million people worldwide living with such a condition. When taken ...

Clinical Trial Growth & Future Outlook: Analysis of the 150+ industry-sponsored siRNA clinical trials conducted between 2020 and 2024, with a 79.5% CAGR reflecting significant industry investment.

February 28 is Rare Disease Day, dedicated to raising awareness for the 300 million individuals globally affected by uncommon illnesses. As such, we take look at one rare ailment which caused ...

Around the world, events are being held to mark Rare Disease Day (28 February 2025), with the aim of bringing attention to rare diseases and improving access to diagnosis and therapies for patients.

Prince Frederik of Luxembourg died from a genetic disease called PolG, but experts hope his passing could bring more awareness to the rare condition that impacted his life. Prince Frederik ...

She announced Arakawa’s cause of death was hantavirus — a rare illness contracted via contact with rodents like rats and mice. Meanwhile, Hackman’s death was tied to heart disease with ...

Because the disease causes such a wide range of symptoms and affects many different organ systems, it can be difficult to diagnose. The prince died a day after Rare Disease Day, an international ...

For millions living with rare diseases, the road to diagnosis and treatment is often filled with uncertainty. It is also ...

(PRNewsfoto/Avidity Biosciences, Inc.) "Rare Disease Day represents an important opportunity for all of us, including people living with rare diseases, their friends, family and caregivers ...