For some families, this is a daily reality due to rare genetic disorders. One such condition is Sanfilippo syndrome, which creates significant hurdles for affected children and their families.
Sanfilippo Syndrome Type A, or MPS IIIA, is a rare, fatal neurodegenerative disease in which the body is unable to break down a complex sugar molecule called heparan sulfate. This disorder ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback