ARTHEx also has ATX-01 in preclinical testing for myotonic dystrophy type 2 (DM2). “Although DM2 is caused by a different mutation, it similarly results in the sequestration of MBNL proteins ...

It usually affects small muscles first, such as those in the: The type of myotonic dystrophy that begins at birth is more serious. Other forms get worse very slowly, and can take 50 or 60 years to ...

The comic's widow, Dara Gottfried, says a portion of sales of 'Still Screaming' will benefit the Gilbert Gottfried Myotonic ...

Dyne CEO Joshua Brumm said that this year the Phase 1/2 studies in myotonic dystrophy type 1 (DM1) and Duchenne muscular dystrophy will each optimize the dose and dose regimen to test in a cohort ...