Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...

An epidemiologist said the Franklin County resolution was "based on conspiracy and misinformation against the COVID-19 ...

Medics in the UK have become the first in the world to successfully administer a pioneering gene therapy that preserves sight ...

This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first ...

This story was originally published by ProPublica. ProPublica is a nonprofit newsroom that investigates abuses of power. Sign up to receive its biggest stories as soon as they’re published.

Christmas has come a few days early for Spark Therapeutics after the FDA approved its ground-breaking gene therapy for a rare eye disease. It looked likely that the FDA would approve the US ...

Get Instant Summarized Text (Gist) Gene therapy and bone marrow transplantation have shown promise in alleviating symptoms of multiple sulfatase deficiency (MSD), a rare genetic disorder. In mouse ...

CSL Behring has shared positive four-year results from a late-stage study of its haemophilia B gene therapy Hemgenix ...

A second gene therapy candidate that spurs antigen-specific ... following myocardial infarction was deemed due to a previous history of coronary artery disease and severe aortic stenosis rather ...