Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA encoding a ...

Jace’s mum DJ, 35, told the PA news agency: “Pre-surgery, at around two years old, you could have held up any object, even a ...

An epidemiologist said the Franklin County resolution was "based on conspiracy and misinformation against the COVID-19 ...

This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first ...

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Christmas has come a few days early for Spark Therapeutics after the FDA approved its ground-breaking gene therapy for a rare eye disease. It looked likely that the FDA would approve the US ...

Get Instant Summarized Text (Gist) Gene therapy and bone marrow transplantation have shown promise in alleviating symptoms of multiple sulfatase deficiency (MSD), a rare genetic disorder. In mouse ...

CSL Behring has shared positive four-year results from a late-stage study of its haemophilia B gene therapy Hemgenix ...