When a test determined that Walter had hemophilia, his Omaha owner joined a group seeking to raise $50,000 for a clinical ...

The first hemophilia B patient at the Loma Linda University Health Hemophilia Treatment Center to receive Hympavzi is a ...

The Omaha resident, who has adopted and fostered a number of dogs, had traveled to the shelter hoping to adopt a Japanese ...

Pfizer opted to discontinue the product for "several reasons," including limited interest from patients and physicians in gene therapies for hemophilia.

DelveInsight's Advanced Therapy Medicinal Products Market Insights report provides the current and forecast market analysis, ...

The expansion of the advanced therapy medicinal products market is primarily fueled by the increasing incidence of chronic diseases. The rising prevalence of genetic disorders and cancer, along ...

Advocates and patients with rare diseases spent Tuesday morning talking with lawmakers and educating the public as part of ...

Under the terms of the cash and stock deal, NewGenIVF is paying $750,000 in cash and issuing 125,000 ordinary shares at $34 ...

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

The Government of Kerala oversees the Kerala State Lotteries program. It was founded in 1967 and is the first of its kind in ...

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为解决血友病 B 治疗难题，韩国研究人员开展 iPSC 源工程肝细胞片治疗血友病 B 的研究。结果显示该细胞片能长时间分泌 FIX 蛋白。这一成果为血友病 B 治疗带来新希望，极具科研价值，推荐大家阅读。