The evidence provided in the manuscript is convincing, with rigorous biochemical assays and state-of-the-art microscopy methods. Becker muscular dystrophy (BMD), an X-linked muscular dystrophy, is ...

People with Duchenne or Becker muscular dystrophy who had more siblings typically report being better prepared to transition to adult life, a study says.

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

I’ve been married for 11 years. Before then, as I grew up with what I eventually discovered was limb-girdle muscular dystrophy, I learned a lot about life, perseverance, and relationships. During my ...

Baron Funds, an investment management company, released its “Baron Health Care Fund” fourth quarter 2024 investor letter. The ...

Edgewise Therapeutics , Inc. (NASDAQ:EWTX), with a market capitalization of $2.67 billion, is a biopharmaceutical company focused on developing innovative therapies for severe, rare muscle disorders.

A cure is not possible with a very small version of the protein, Kelly explained, so the goal of current gene therapies is not to cure but to transform DMD into the less severe Becker muscular ...

Managed Healthcare Executive provides C-suite executives at health plans and provider organizations with news, analysis, ...