Scholar Rock is asking the U.S. Food and Drug Administration to approve apitegromab for people with spinal muscular atrophy.

Inclement weather can pose a threat to people like columnist Ari Anderson, who depend on in-home care. Such are the storms of ...

Columnist Helen Baldwin gains a different perspective following a crushing diagnosis, but glasses weren't what helped her to see clearly.

Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.

Icy paths and cold temperatures pose challenges for columnist Kevin Schaefer, a power wheelchair user who's living with SMA.

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

Regulators in the U.S. and the European Union agreed to review Biogen’s applications for approval of a higher dose Spinraza ...

A woman with SMA type 3 became pregnant while on Spinraza treatment and gave birth to a healthy child, per a case report.

Nonadherence by SMA patients to their prescribed regimen of Evrysdi is linked to higher healthcare costs, a real-world U.S.

Columnist Alyssa Silva is recovering from a dangerous respiratory illness. With SMA, that means a whole lot more than it does ...

Last year brought more doctor appointments than usual for columnist Halsey Blocher, who already sees her SMA medical team regularly.